Inborn errors of metabolism Disease

About Gene:

Inborn errors of metabolism is a rare genetic disorder. Patients with the disorder are unable to efficiently extract energy from food.

Number of Patients: 0

Disease Causing Genes:

Sign and Symptoms:

  1. Fructose intolerance
  2. Galactosemia
  3. Maple syrup urine disease (MSUD)
  4. Phenyletouira
  5. Fatty acid oxidation defects
  6. Lysosomal storage disorders
  7. Mitochondrial disorder

Diagnosis:

(1) Medical history collection (2) Screening of amino acid, organic acid, and fatty acid metabolism disorders by tandem mass spectrometry

Preventions:

Treatment:

Symptomatic treatments are administrated based on circumstances